Help us fund the cure.
Help Jack, and thousands of other children living with a SCN2A gene mutation. Because no child should not be deemed “too rare to care”.
Donate Today
All funds raised support our active gene therapy project and the work required to develop the first ever gene therapy treatment for SCN2A.
Not someday - but urgently.
Every contribution counts.
Donate securely below.
Powered by Raisely
Making a larger donation?
To reduce transaction fees and ensure more of your donation goes toward our gene therapy work, we welcome direct bank transfers.
Your support helps fund the work required to advance a gene therapy treatment for SCN2A, including:
Scientific and pre-clinical research
Translational and therapeutic development
Manufacturing and regulatory readiness
Clinical planning and early-stage trials
The operational and fundraising work that makes this progress possible
This work doesn’t stop with SCN2A. By helping move gene therapy forward, you are opening doors for other rare genetic conditions - proving that no child is “too rare” to matter.